245. プロピオン酸血症 Propionic acidemia Clinical trials / Disease details


臨床試験数 : 13 薬物数 : 16 - (DrugBank : 3) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 6

  
1 trial found
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enrollment
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agemin
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agemax
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PhaseCountries
1NCT04836494
(ClinicalTrials.gov)
March 25, 202129/3/2021A First in Human, Dose Escalation Study to Evaluate the Safety and Tolerability of BBP-671 in Healthy Volunteers and Patients With Propionic Acidemia or Methylmalonic AcidemiaA First-in-human, Randomized, Placebo-controlled, Single and Multiple Ascending Dose Escalation to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BBP-671 in Healthy Subjects and In Patients With Propionic Acidemia or Methylmalonic AcidemiaHealthy Volunteers;Propionic Acidemia;Methylmalonic Acidemia;Organic AcidemiaDrug: BBP-671;Drug: PlaceboCoA Therapeutics, Inc., a BridgeBio companyNULLRecruiting15 Years55 YearsAll128Phase 1United States