251. 尿素サイクル異常症 Urea cycle disorder Clinical trials / Disease details


臨床試験数 : 54 薬物数 : 61 - (DrugBank : 15) / 標的遺伝子数 : 3 - 標的パスウェイ数 : 28

  
1 trial found
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agemin
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1NCT03179878
(ClinicalTrials.gov)
June 16, 20176/6/2017Safety and Tolerability of SYNB1020-CP-001A Phase 1, First-in-human, Oral Single and Multiple Dose-Escalation, Randomized, Double-blinded, Placebo-controlled Study of SYNB1020 in Healthy Adult Volunteers to Evaluate Safety, Tolerability, Dosing, and PharmacodynamicsHealthy Volunteer;Urea Cycle DisorderDrug: Placebo;Drug: SYNB1020SynlogicNULLCompleted18 Years64 YearsAll52Phase 1United States