DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
254. ポルフィリン症
Porphyria
Clinical trials
/
Disease details
臨床試験数
:
72
/
薬物数
:
53
- (
DrugBank
:
16
) /
標的遺伝子数
:
19
-
標的パスウェイ数
:
35
Search
2 trials found
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No.
TrialID
Date_
enrollment
Date_
registration
Public_title
Scientific_title
Condition
Intervention
Primary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
Phase
Countries
1
NCT02922413
(
ClinicalTrials.gov
)
October 30, 2015
1/1/2016
Panhematin for Prevention of Acute Attacks of Porphyria
Safety and Efficacy of Panhematin™ for Prevention of Acute Attacks of Porphyria
Acute Intermittent Porphyria;Hereditary Coproporphyria;Variegate Porphyria
Biological:
Hemin
for injection
;Other: Placebo
The University of Texas Medical Branch, Galveston
NULL
Recruiting
18 Years
N/A
All
20
Phase 2
United States
2
NCT02935400
(
ClinicalTrials.gov
)
April 28, 2014
13/10/2016
Acute Porphyria Biomarkers for Disease Activity
Acute Porphyrias: Biomarkers for Disease Activity and Response to Treatment
Acute Intermittent Porphyria;Hereditary Coproporphyria;Variegate Porphyria
Drug:
Hemin
The University of Texas Medical Branch, Galveston
NULL
Active, not recruiting
18 Years
N/A
All
50
United States