254. ポルフィリン症 Porphyria Clinical trials / Disease details


臨床試験数 : 72 薬物数 : 53 - (DrugBank : 16) / 標的遺伝子数 : 19 - 標的パスウェイ数 : 35

  
1 trial found
No.TrialIDDate_
enrollment
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agemin
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agemax
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PhaseCountries
1NCT02922413
(ClinicalTrials.gov)
October 30, 20151/1/2016Panhematin for Prevention of Acute Attacks of PorphyriaSafety and Efficacy of Panhematin™ for Prevention of Acute Attacks of PorphyriaAcute Intermittent Porphyria;Hereditary Coproporphyria;Variegate PorphyriaBiological: Hemin for injection;Other: PlaceboThe University of Texas Medical Branch, GalvestonNULLRecruiting18 YearsN/AAll20Phase 2United States