255. 複合カルボキシラーゼ欠損症 Multiple carboxylase deficiency Clinical trials / Disease details


臨床試験数 : 1 薬物数 : 1 - (DrugBank : 0) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0

  
1 trial found
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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sponsor
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Status
Inclusion_
agemin
Inclusion_
agemax
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gender
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size
PhaseCountries
1NCT03269045
(ClinicalTrials.gov)
August 31, 201328/8/2017Study of ORL-1B in Patients With Biotinidase DeficiencyAn Open-label, Single-arm, Phase 2 Study of ORL-1B in Patients With Biotinidase DeficiencyBiotinidase DeficiencyDrug: ORL-1BOrpha LabsNULLCompletedN/A18 YearsAll20Phase 1/Phase 2NULL