256. 筋型糖原病 Muscle glycogenosis Clinical trials / Disease details
臨床試験数 : 180 / 薬物数 : 133 - (DrugBank : 29) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 105
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT02824068 (ClinicalTrials.gov) | June 1, 2016 | 20/6/2016 | Long-term Outcome in Late-onset Pompe Disease Treated Beyond 36 Months (STIG-Pompe-Study) | Long-term Outcome in Late-onset Pompe Disease Treated Beyond 36 Months | Pompe Disease | Drug: glucosidase alfa | Klinikum der Universitaet Muenchen | Genzyme, a Sanofi Company | Completed | 8 Years | N/A | All | 112 | Germany;Italy;Taiwan;Argentina;Brazil |