256. 筋型糖原病 Muscle glycogenosis Clinical trials / Disease details


臨床試験数 : 180 薬物数 : 133 - (DrugBank : 29) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 105

  
1 trial found
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agemin
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1NCT04226274
(ClinicalTrials.gov)
December 10, 20199/1/2020A Study of the Safety of REN001 in Patients With McArdle DiseaseA Phase 1b, Open-label Study to Evaluate the Safety and Tolerability of 12 Weeks Treatment With Oral REN001 in Patients With McArdle Disease (Glycogen Storage Disorder 5)McArdle DiseaseDrug: REN001Reneo Pharma LtdNULLCompleted18 YearsN/AAll19Phase 1Spain;United Kingdom