285. ファンコニ貧血 Fanconi anemia Clinical trials / Disease details
臨床試験数 : 62 / 薬物数 : 93 - (DrugBank : 30) / 標的遺伝子数 : 30 - 標的パスウェイ数 : 144
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT03351868 (ClinicalTrials.gov) | December 1, 2017 | 20/11/2017 | FANCA Gene Transfer for Fanconi Anemia Using a High-safety, High-efficiency, Self-inactivating Lentiviral Vector | Gene Transfer for Fanconi Anemia Using a Self-inactivating Lentiviral Vector | Fanconi Anemia | Genetic: Gene-modified autologous stem cells | Shenzhen Geno-Immune Medical Institute | NULL | Recruiting | 2 Years | 20 Years | All | 10 | N/A | China |