3. 脊髄性筋萎縮症 Spinal muscular atrophy Clinical trials / Disease details


臨床試験数 : 237 薬物数 : 123 - (DrugBank : 29) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 75

  
1 trial found
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agemin
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agemax
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PhaseCountries
1NCT05614531
(ClinicalTrials.gov)
November 1, 20222/11/2022Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients With Spinal Muscular Atrophy Type 1A Multicenter, Nonrandomized, Open-label,Dose Escalation Clinical Trial to Assess the Safety and Efficacy of EXG001 307 After Intravenous Injection in Patients With Spinal Muscular Atrophy Type 1Spinal Muscular Atrophy Type IGenetic: EXG001-307 injectionHangzhou Jiayin Biotech LtdNULLRecruiting1 Day180 DaysAll12Phase 1/Phase 2China