3. 脊髄性筋萎縮症 Spinal muscular atrophy Clinical trials / Disease details


臨床試験数 : 237 薬物数 : 123 - (DrugBank : 29) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 75

  
3 trials found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT00439569
(ClinicalTrials.gov)
January 200821/2/2007Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Types II or IIIPhase I/IIa Clinical Trial of Sodium Phenylbutyrate in Pediatric Subjects With Type II/III Spinal Muscular AtrophySpinal Muscular Atrophy Type II;Spinal Muscular Atrophy Type IIIDrug: sodium phenylbutyrateWestatNational Institute of Neurological Disorders and Stroke (NINDS)Terminated2 Years11 YearsAll9Phase 1/Phase 2United States
2NCT00439218
(ClinicalTrials.gov)
January 200822/2/2007Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type IPhase I/IIa Clinical Trial of Sodium Phenylbutyrate in Pediatric Subjects With Type I Spinal Muscular AtrophySpinal Muscular Atrophy Type IDrug: sodium phenylbutyrateWestatNational Institute of Neurological Disorders and Stroke (NINDS)Terminated2 Months48 MonthsAll5Phase 1/Phase 2United States
3NCT00528268
(ClinicalTrials.gov)
July 200710/9/2007Study to Evaluate Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular AtrophyProspective Phase I/II Study to Evaluate Effects of Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular AtrophySpinal Muscular AtrophyDrug: Sodium phenylbutyrate (NaPB)University of UtahEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)CompletedN/A6 MonthsAll14Phase 1/Phase 2United States