307. カナバン病 Canavan disease Clinical trials / Disease details


臨床試験数 : 6 薬物数 : 11 - (DrugBank : 5) / 標的遺伝子数 : 2 - 標的パスウェイ数 : 2

  
1 trial found
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1NCT05317780
(ClinicalTrials.gov)
February 10, 202024/3/2022Canavan-Single Patient INDExpanded Access Trial of Systemic Delivery of Aspartoacylase ASPA (rAAV9-CB6-AspA) Gene Vector in a Single Patient With Canavan DiseaseCanavan DiseaseDrug: rAAV9-CB6-AspABarry J. ByrneUniversity of Miami;University of Massachusetts, WorcesterAvailable18 Months24 MonthsMaleUnited States