329. 無虹彩症 Aniridia Clinical trials / Disease details

臨床試験数 : 3 / 薬物数 : 2 - (DrugBank : 2) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0

2 trials found

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04117880 (ClinicalTrials.gov)	December 31, 2018	19/9/2019	A Phase 2 Open Label Extension Study in Participants With Nonsense Mutation Aniridia	Nonsense Mutation Aniridia: An Ataluren (PTC124) Phase 2 Extension Study	Aniridia	Drug: Ataluren	PTC Therapeutics	NULL	Withdrawn	2 Years	N/A	All	0	Phase 2	NULL
2	NCT02647359 (ClinicalTrials.gov)	January 31, 2016	29/12/2015	Study of Ataluren in Participants With Nonsense Mutation Aniridia	STAR: A Phase 2, Multicenter, Randomized, Double-Masked, Placebo-Controlled Study of the Safety and Efficacy of Ataluren (PTC124) for the Treatment of Nonsense Mutation Aniridia	Aniridia	Drug: Ataluren;Drug: Placebo	PTC Therapeutics	NULL	Completed	2 Years	N/A	All	39	Phase 2	United States;Canada