65. 原発性免疫不全症候群 Primary immunodeficiency Clinical trials / Disease details
臨床試験数 : 500 / 薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT01347346 (ClinicalTrials.gov) | May 2011 | 3/5/2011 | Gene Therapy for WAS | Phase I/II Clinical Trial of Haematopoietic Stem Cell Gene Therapy for the Wiskott-Aldrich Syndrome | Wiskott-Aldrich Syndrome | Genetic: Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene | Genethon | Hôpital Necker-Enfants Malades | Completed | N/A | N/A | Male | 5 | Phase 1/Phase 2 | France |
| 2 | NCT01347242 (ClinicalTrials.gov) | March 2011 | 3/5/2011 | Gene Therapy for Wiskott-Aldrich Syndrome (WAS) | Phase I/II Clinical Trial of Haematopoietic Stem Cell Gene Therapy for the Wiskott-Aldrich Syndrome | Wiskott-Aldrich Syndrome | Genetic: Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene | Genethon | Great Ormond Street Hospital for Children NHS Foundation Trust;Institute of Child Health | Completed | N/A | N/A | Male | 6 | Phase 1/Phase 2 | United Kingdom |