DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
65. 原発性免疫不全症候群
Primary immunodeficiency
Clinical trials
/
Disease details
臨床試験数
:
500
/
薬物数
:
614
- (
DrugBank
:
119
) /
標的遺伝子数
:
92
-
標的パスウェイ数
:
217
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No.
TrialID
Date_
enrollment
Date_
registration
Public_title
Scientific_title
Condition
Intervention
Primary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
Phase
Countries
1
NCT03645486
(
ClinicalTrials.gov
)
July 1, 2018
24/7/2018
Lentiviral Gene Therapy for CGD
Lentiviral Gene Therapy for Chronic Granulomatous Disease (CGD)
Chronic Granulomatous Disease
Genetic:
Infusion of lentiviral TYF-CGD-modified autologous stem cells
Shenzhen Geno-Immune Medical Institute
NULL
Recruiting
N/A
N/A
All
10
N/A
China