DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
65. 原発性免疫不全症候群
Primary immunodeficiency
Clinical trials
/
Disease details
臨床試験数
:
500
/
薬物数
:
614
- (
DrugBank
:
119
) /
標的遺伝子数
:
92
-
標的パスウェイ数
:
217
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No.
TrialID
Date_
enrollment
Date_
registration
Public_title
Scientific_title
Condition
Intervention
Primary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
Phase
Countries
1
NCT03601286
(
ClinicalTrials.gov
)
December 21, 2018
22/2/2018
Lentiviral Gene Therapy for X-linked Severe Combined Immunodeficiency
Phase I/II Study of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan
Severe Combined Immunodeficiency, X-Linked
Drug:
Lentiviral vector transduced CD34+ cells
Great Ormond Street Hospital for Children NHS Foundation Trust
NULL
Recruiting
8 Weeks
5 Years
Male
5
Phase 1
United Kingdom
2
NCT01381003
(
ClinicalTrials.gov
)
November 2011
23/6/2011
Lentiviral Gene Therapy for X-Linked Chronic Granulomatous Disease (X-CGD)
Phase I/II Gene Therapy Protocol for X-Linked Chronic Granulomatous Disease
Granulomatous Disease, Chronic, X-linked, Variant
Genetic:
pCCLchimGp91s
lentiviral vector transduced CD34+ cells
infusion
Great Ormond Street Hospital for Children NHS Foundation Trust
NULL
Withdrawn
N/A
30 Years
Male
0
Phase 1/Phase 2
United Kingdom