65. 原発性免疫不全症候群 Primary immunodeficiency Clinical trials / Disease details


臨床試験数 : 500 薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217

  
1 trial found
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enrollment
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agemin
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PhaseCountries
1EUCTR2007-000684-16-GB
(EUCTR)
21/01/201017/09/2009Gene therapy for SCID-X1 using a self-inactivating (SIN) gammaretroviral vector. - Gene therapy for SCID-X1Gene therapy for SCID-X1 using a self-inactivating (SIN) gammaretroviral vector. - Gene therapy for SCID-X1 X-Linked severe combined Immunodeficiency (SCID-X1)
MedDRA version: 9.1;Level: LLT;Classification code 10010099;Term: Combined immunodeficiency
Product Name: pSRS11.EFS.IL2RG.pre* retroviral vector
Product Code: pSRS11.EFS.IL2RG.pre* retroviral vector
Product Name: pSRS11.EFS.IL2RG.pre* retroviral vector transduced cells
Product Code: pSRS11.EFS.IL2RG.pre* retroviral vector transduce
Great Ormond Street Hospital NHS Trust / University College London - Institute of Child HealthNULLNot RecruitingFemale: no
Male: yes
10Phase 1;Phase 2United Kingdom