65. 原発性免疫不全症候群 Primary immunodeficiency Clinical trials / Disease details

臨床試験数 : 500 / 薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217

24 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04965597 (ClinicalTrials.gov)	April 19, 2022	21/6/2021	Treosulfan-Based Conditioning Regimen Before a Blood or Bone Marrow Transplant for the Treatment of ...	Hematopoietic Cell Transplantation Using Treosulfan-Based Conditioning for the Treatment of Bone Mar ...	Bone Marrow Failure Syndrome;Congenital Amegakaryocytic Thrombocytopenia;Congenital Pure Red Cell Ap ...	Drug: Treosulfan;Drug: Fludarabine Phosphate;Drug: Tacrolimus;Drug: Methotrexate;Biological: Lapine ...	Fred Hutchinson Cancer Center	Blood and Marrow Transplant Clinical Trials Network;National Cancer Institute (NCI);National Marrow ...	Recruiting	1 Year	49 Years	All	40	Phase 2	United States
2	EUCTR2018-000338-36-IT (EUCTR)	12/05/2021	04/06/2021	Open-label, Long-term, Extension Treatment using Intra-Erythrocyte Dexamethasone Sodium Phosphatein ...	Open-label, Long-term, Extension Treatment using Intra-Erythrocyte Dexamethasone Sodium Phosphatein ...	Neurological symptoms of Ataxia Telangiectasia MedDRA version: 21.0;Level: PT;Classification code 10 ...	Product Name: Dexamethasone sodium phosphate (soluzione 25mg/ml) Product Code: [Dexamethasone sodium pho ...	ERYDEL S.P.A.	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	155	Phase 3	United States;Spain;Poland;Belgium;Australia;Norway;Germany;Tunisia;United Kingdom;Italy;India
3	EUCTR2018-000338-36-NO (EUCTR)	06/11/2020	04/02/2020	Not Applicable	Open-label, Long-term, Extension Treatment using Intra-Erythrocyte Dexamethasone Sodium Phosphatein ...	Patient with neurological symptoms of Ataxia Telangiectasia MedDRA version: 21.0;Level: PT;Classific ...	Product Name: Dexamethasone sodium phosphate INN or Proposed INN: Dexamethasone sodium phosphate Other d ...	EryDel S.p.A.	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	155	Phase 3	United States;Spain;Poland;Belgium;Australia;Tunisia;Germany;Norway;United Kingdom;Italy;India
4	EUCTR2018-000338-36-GB (EUCTR)	27/05/2020	20/01/2020	Not Applicable	Open-label, Long-term, Extension Treatment using Intra-Erythrocyte Dexamethasone Sodium Phosphatein ...	Patient with neurological symptoms of Ataxia Telangiectasia MedDRA version: 21.0;Level: PT;Classific ...	Product Name: Dexamethasone sodium phosphate INN or Proposed INN: Dexamethasone sodium phosphate Other d ...	EryDel S.p.A.	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	51	Phase 3	United States;Spain;Poland;Belgium;Australia;Israel;Norway;Germany;United Kingdom;India
5	EUCTR2018-004191-35-BE (EUCTR)	12/04/2019	05/03/2019	Use of an antidiabetic drug (Empagliflozin) to lower the blood level of 1,5-anhydroglucitol in patie ...	Evaluation of the safety and efficacy of administration of Empagliflozin in a new treatment for neut ...	(1) Severe Congenital Neutropenia type 4 (SNC4) due to a deficiency in G6PC3, a phosphatase of the e ...	Trade Name: Jardiance Product Name: Empagliflozin Product Code: A10BK03	Cliniques universitaires Saint-Luc	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	5	Phase 4	Belgium
6	EUCTR2018-000338-36-DE (EUCTR)	20/09/2018	21/06/2018	Not Applicable	Open-label, Long-term, Extension Treatment using Intra-Erythrocyte Dexamethasone Sodium Phosphatein ...	Patient with neurological symptoms of Ataxia Telangiectasia MedDRA version: 21.0;Level: PT;Classific ...	Product Name: Dexamethasone sodium phosphate INN or Proposed INN: Dexamethasone sodium phosphate Other d ...	EryDel S.p.A.	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	150	Phase 3	United States;Spain;Poland;Belgium;Australia;Israel;Norway;Germany;United Kingdom;India
7	EUCTR2018-000338-36-BE (EUCTR)	23/08/2018	28/06/2018	Not Applicable	Open-label, Long-term, Extension Treatment using Intra-Erythrocyte Dexamethasone Sodium Phosphatein ...	Patient with neurological symptoms of Ataxia Telangiectasia MedDRA version: 20.1;Level: PT;Classific ...	Product Name: Dexamethasone sodium phosphate INN or Proposed INN: Dexamethasone sodium phosphate Other d ...	EryDel S.p.A.	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	51	Human pharmacology (Phase 1): no Therapeutic exploratory (Phase 2): no Therapeutic confirmatory - (P ...	United States;Poland;Spain;Belgium;Australia;Israel;Germany;India
8	EUCTR2018-000338-36-ES (EUCTR)	31/05/2018	05/04/2018	Not Applicable	Open-label, Long-term, Extension Treatment using Intra-Erythrocyte Dexamethasone Sodium Phosphatein ...	Patient with neurological symptoms of Ataxia Telangiectasia MedDRA version: 20.1;Level: PT;Classific ...	Product Name: Dexamethasone sodium phosphate INN or Proposed INN: Dexamethasone sodium phosphate Other d ...	EryDel S.p.A.	NULL	Authorised-recruitment may be ongoing or finished			Female: yes Male: yes	61	Phase 3	United States;Poland;Belgium;Spain;Australia;Israel;Norway;Germany;Italy;United Kingdom;India
9	NCT03333486 (ClinicalTrials.gov)	December 7, 2017	2/11/2017	Fludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in T ...	A Phase II Trial of Haploidentical Allogeneic Stem Cell Transplantation Utilizing Mobilized Peripher ...	Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive;Acute Leukemia in Remission;Acute ...	Drug: Cyclophosphamide;Drug: Fludarabine Phosphate;Other: Laboratory Biomarker Analysis;Procedure: P ...	Roswell Park Cancer Institute	NULL	Active, not recruiting	1 Year	75 Years	All	31	Phase 2	United States
10	NCT02770807 (ClinicalTrials.gov)	March 2, 2017	2/5/2016	EDS in Ataxia Telangiectasia Patients	Multi-center, Randomized, Double-blind, Placebo-controlled Trial to Evaluate the Effects of Intra-Er ...	Nervous System Disease;Genetic Syndrome	Drug: EDS-EP dose range of ~5-10 mg DSP/infusion;Drug: EDS-EP dose range of ~14-22 mg DSP/infusion;D ...	Erydel	NULL	Completed	6 Years	N/A	All	175	Phase 3	United States;Australia;Belgium;Germany;India;Israel;Italy;Norway;Poland;Spain;Tunisia;United Kingdo ...

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