Evaluating the Effectiveness of STRIMVELIS Risk Minimization Measures (RMMs)
Evaluation of Referring HCPs' and Parents'/Carers' Understanding of Specific Risks Associated With Strimvelis™ Treatment Evaluation of Referring HCPs' and Parents'/Carers' Understanding of Specific Risks Associated With S ...
Severe Combined Immunodeficiency Due to ADA Deficiency
Methodology study to investigate the utility of retroviral insertion site analysis in samples from subjects treated with Strimvelis™ gene therapy - Retroviral insertion site methodology study Methodology study to investigate the utility of retroviral insertion site analysis in samples from s ...
Adenosine deaminase (ADA) deficiency severe combined immunodeficiency MedDRA version: 20.1;Level: LLT;Classification code 10066367;Term: Adenosine deaminase deficiency;System Organ Class: 100000004850;Therapeutic area: Diseases [C] - Immune System Diseases [C20] Adenosine deaminase (ADA) deficiency severe combined immunodeficiency MedDRA version: 20.1;Level: LL ...
Strimvelis Registry Study to Follow-up Patients With Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID) StrimvelisRegistry Study to Follow-up Patients With Adenosine Deaminase Severe Combined Immunodefici ...
Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID) Registry for Patients Treated With Strimvelis (Previously GSK2696273) Gene Therapy: Long-Term Prospective, Non-Interventional Follow-up of Safety and Effectiveness Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID) Registry for Patients Treated With S ...