65. 原発性免疫不全症候群 Primary immunodeficiency Clinical trials / Disease details
臨床試験数 : 500 / 薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT01175239 (ClinicalTrials.gov) | April 2011 | 29/7/2010 | Gene Therapy for X-linked Severe Combined Immunodeficiency (SCID-X1) | Gene Therapy for SCID-X1 Using a Self-inactivating (SIN) Gammaretroviral Vector | X-linked Severe Combined Immunodeficiency | Genetic: Single infusion of autologous CD34+ cells transduced with the self-inactivating (SIN) gammaretroviral vector pSRS11.EFS.IL2RG.pre | Great Ormond Street Hospital for Children NHS Foundation Trust | NULL | Active, not recruiting | N/A | 16 Years | Male | 1 | N/A | United Kingdom |