79. 家族性高コレステロール血症(ホモ接合体) Homozygous familial hypercholesterolemia Clinical trials / Disease details


臨床試験数 : 145 薬物数 : 114 - (DrugBank : 26) / 標的遺伝子数 : 8 - 標的パスウェイ数 : 17

  
1 trial found
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1NCT05217667
(ClinicalTrials.gov)
April 22, 202220/1/2022Study of ARO-ANG3 in Participants With Homozygous Familial Hypercholesterolemia (HOFH)Phase 2 Study to Evaluate the Safety and Efficacy of ARO-ANG3 in Subjects With Homozygous Familial Hypercholesterolemia (HOFH)Homozygous Familial HypercholesterolemiaDrug: ARO-ANG 3 InjectionArrowhead PharmaceuticalsNULLActive, not recruiting16 YearsN/AAll18Phase 2United States;Australia;Canada;South Africa