79. 家族性高コレステロール血症（ホモ接合体） Homozygous familial hypercholesterolemia Clinical trials / Disease details

臨床試験数 : 145 / 薬物数 : 114 - (DrugBank : 26) / 標的遺伝子数 : 8 - 標的パスウェイ数 : 17

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2016-001446-25-IT (EUCTR)	02/10/2017	06/05/2021	This is a study to investigate if gene therapy is safe in people with homozygous familial hyperchole ...	AAV8-mediated Low Density Lipoprotein Receptor (LDLR) Gene Replacement in Subjects with Homozygous F ...	Adults with homozygous familial hypercholesterolemia;Therapeutic area: Diseases [C] - Cardiovascular ...	Product Name: AAV8.TBG.hLDLR Product Code: AAV8.TBG.hLDLR Product Name: prednisone Product Code: predni ...	REGENXBIO Inc.	NULL	Not Recruiting			Female: yes Male: yes	12	Phase 1;Phase 2	United States;Canada;Netherlands;Italy

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