90. 網膜色素変性症 Retinitis pigmentosa Clinical trials / Disease details


臨床試験数 : 147 薬物数 : 176 - (DrugBank : 43) / 標的遺伝子数 : 49 - 標的パスウェイ数 : 110

  
1 trial found
No.TrialIDDate_
enrollment
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registration
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Inclusion_
agemin
Inclusion_
agemax
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gender
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PhaseCountries
1NCT04312672
(ClinicalTrials.gov)
February 18, 201915/7/2019Long Term Follow-Up Gene Therapy Study for XLRP RPGRLong Term Follow-Up Study of Participants Following an Open Label, Multi-Centre, Phase I/II Dose Escalation Trial of a Recombinant Adeno-Associated Virus Vector (AAV2-RPGR) for Gene Therapy of Adults and Children With X-Linked Retinitis Pigmentosa Owing to Defects in Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaBiological: AAV-RPGRMeiraGTx UK II LtdNULLRecruiting5 YearsN/AMale36Phase 1/2United States;United Kingdom