90. Retinitis pigmentosa Clinical trials / Disease details


Clinical trials : 147 Drugs : 176 - (DrugBank : 43) / Drug target genes : 49 - Drug target pathways : 110

  
1 trial found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT03252847
(ClinicalTrials.gov)
July 14, 20171/8/2017Gene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)An Open Label, Multi-centre, Phase I/II Dose Escalation Trial of a Recombinant Adeno-associated Virus Vector (AAV2-.RPGR) for Gene Therapy of Adults and Children With X-linked Retinitis Pigmentosa Owing to Defects in Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaGenetic: AAV2/5-RPGRMeiraGTx UK II LtdSyne Qua Non Limited;Bionical EmasCompleted5 YearsN/AMale49Phase 1/Phase 2United States;United Kingdom