90. Retinitis pigmentosa Clinical trials / Disease details


Clinical trials : 147 Drugs : 176 - (DrugBank : 43) / Drug target genes : 49 - Drug target pathways : 110

  
1 trial found
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1NCT05203939
(ClinicalTrials.gov)
January 24, 202216/11/2021The Study to Assess the Safety and Efficacy of OCU400 for Retinitis Pigmentosa and Leber Congenital AmaurosisPhase 1/2 Study to Assess the Safety and Efficacy of Ocu400 for Retinitis Pigmentosa Associated With Nr2e3 and Rho Mutations and Leber Congenital Amaurosis With Mutation(S) in Cep290 GeneRetinitis Pigmentosa;Leber Congenital AmaurosisDrug: OCU400 Low Dose;Drug: OCU400 Mid Dose;Drug: OCU400 High DoseOcugenNULLRecruiting18 YearsN/AAll21Phase 1/Phase 2United States