Golodirsen 50 MG/1 ML Intravenous Solution [VYONDYS 53] ( DrugBank: Golodirsen )

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1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
113	筋ジストロフィー	1

113. 筋ジストロフィー

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臨床試験数 : 646 /  薬物数 : 471 - (DrugBank : 105) / 標的遺伝子数 : 59 - 標的パスウェイ数 : 170

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04708314 (ClinicalTrials.gov)	October 31, 2020	21/9/2020	An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular Dystrophy	An Open-Label Study to Evaluate the Safety of Golodirsen in Non-Ambulant Patients With Duchenne Muscular Dystrophy	Duchenne Muscular Dystrophy	Drug: Golodirsen 50 MG/1 ML Intravenous Solution [VYONDYS 53]	Rare Disease Research, LLC	Sarepta Therapeutics, Inc.	Terminated	7 Years	N/A	Male	2	Phase 4	United States