PBFT02 ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
127前頭側頭葉変性症1

127. 前頭側頭葉変性症


臨床試験数 : 90 薬物数 : 87 - (DrugBank : 30) / 標的遺伝子数 : 39 - 標的パスウェイ数 : 88
No.TrialIDDate_
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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Inclusion_
agemin
Inclusion_
agemax
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size
PhaseCountries
1NCT04747431
(ClinicalTrials.gov)
September 14, 20212/2/2021A Study of PBFT02 in Patients With Frontotemporal Dementia and Progranulin Mutations (FTD-GRN)A Phase 1b Open-Label, Multicenter, Dose-Escalation Study to Assess the Safety, Tolerability, and Pharmacodynamic Effects of a Single Dose of PBFT02 Delivered Into the Cisterna Magna of Adult Subjects With Frontotemporal Dementia and Mutations in the Progranulin GeneFrontotemporal DementiaDrug: PBFT02Passage Bio, Inc.NULLRecruiting35 Years75 YearsAll15Phase 1/Phase 2United States;Brazil;Canada;Italy;Portugal;United Kingdom