A Long-Term Extension Study of AT2101 (Afegostat Tartrate) in Type 1 Gaucher Patients
An Open-Label, Multicenter, Long-Term Extension Study To Assess The Safety, Efficacy, And Pharmacodynamics Of AT2101 In Adult Patients With Type 1 Gaucher Disease An Open-Label, Multicenter, Long-Term Extension Study To Assess The Safety, Efficacy, And Pharmacody ...
Gaucher Disease;Type 1 Gaucher Disease;Gaucher Disease, Type 1
An open-label, multicentre, long-term extension study to assess the safety, efficacy and pharmacodynamics of AT2101 in adult patients with Type I Gaucher disease. An open-label, multicentre, long-term extension study to assess the safety, efficacy and pharmacodyn ...
An open-label, multicentre, long-term extension study to assess the safety, efficacy and pharmacodynamics of AT2101 in adult patients with Type I Gaucher disease. An open-label, multicentre, long-term extension study to assess the safety, efficacy and pharmacodyn ...
Type I Gaucher Disease MedDRA version: 9.1;Level: LLT;Classification code 10018048;Term: Gaucher's disease Type I Gaucher Disease MedDRA version: 9.1;Level: LLT;Classification code 10018048;Term: Gaucher's d ...
Product Name: afegostat tartrate Product Code: AT2101 INN or Proposed INN: afegostat tartrate
A Study of Oral AT2101 (Afegostat Tartrate) in Treatment-naive Patients With Gaucher Disease
A Randomized, Open-label Study To Assess the Safety and Tolerability of AT2101 in Treatment-naive Adult Patients With Type 1 Gaucher Disease A Randomized, Open-label Study To Assess the Safety and Tolerability of AT2101 in Treatment-naive Ad ...
Gaucher Disease;Type 1 Gaucher Disease;Gaucher Disease, Type 1
Drug: afegostat tartrate
Amicus Therapeutics
NULL
Completed
18 Years
74 Years
All
19
Phase 2
United States;Israel;South Africa;United Kingdom;Germany
A Study of AT2101 (Afegostat Tartrate) in Adult Patients With Type 1 Gaucher Disease Currently Receiving Enzyme Replacement Therapy A Study of AT2101 (AfegostatTartrate) in Adult Patients With Type 1 Gaucher Disease Currently Receiv ...
A Randomized, Open-label Study to Assess the Safety and Tolerability of Multiple Dose Levels and Multiple Dosing Regimens of AT2101 in Adult Patients With Type 1 Gaucher Disease Currently Receiving Enzyme Replacement Therapy A Randomized, Open-label Study to Assess the Safety and Tolerability of Multiple Dose Levels and Mul ...
Gaucher Disease, Type 1;Type 1 Gaucher Disease;Gaucher Disease