Autologous Plasmablasts (B cells) ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
19ライソゾーム病1

19. ライソゾーム病


臨床試験数 : 899 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT05682144
(ClinicalTrials.gov)
January 15, 202312/12/2022ISP-001: Sleeping Beauty Transposon-Engineered B Cells for MPS IA Phase I Open Label Study to Evaluate the Safety and Tolerability of ISP-001 in Adult Patients With Mucopolysaccharidosis Type I Hurler-Scheie and ScheieMucopolysaccharidosis IH/S;Mucopolysaccharidosis ISBiological: Autologous Plasmablasts (B cells)Immusoft CorporationNULLNot yet recruiting18 YearsN/AAll2Phase 1United States