Evaluation of Intravenous Laronidase Pharmacokinetics Before and After Hematopoietic Cell Transplantation in Patients With Mucopolysaccharidosis Type IH. Evaluation of Intravenous Laronidase Pharmacokinetics Before and After Hematopoietic Cell Transplant ...
Evaluation of Intravenous Laronidase Pharmacokinetics Before and After Hematopoietic Cell Transplantation in Patients With Mucopolysaccharidosis Type IH. Evaluation of Intravenous Laronidase Pharmacokinetics Before and After Hematopoietic Cell Transplant ...
Hematopoietic Cell Transplantation;Mucopolysaccharidosis Type I
Drug: Laronidase therapy and a stem cell transplant