Carbaglu ( DrugBank: - )

2 diseases

告示番号	疾患名（ページ内リンク）	臨床試験数
245	プロピオン酸血症	5
246	メチルマロン酸血症	5

245. プロピオン酸血症

臨床試験数 : 13 / 薬物数 : 16 - (DrugBank : 3) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 6

diseases per page:

Showing 1 to 5 of 5 diseases

Filter by

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT05040178 (ClinicalTrials.gov)	June 30, 2022	16/6/2021	An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics	A Non-Interventional Post-Authorization Safety Study (PASS) of Carbaglu® for the Treatment of Hypera ...	Hyperammonemia;Methylmalonic Acidemia;Propionic Acidemia	Drug: Carglumic Acid	Recordati Rare Diseases	Target PharmaSolutions, Inc.	Recruiting	N/A	N/A	All	20		United States
2	NCT04284917 (ClinicalTrials.gov)	November 28, 2019	24/2/2020	Long-term Efficacy of Carglumic Acid in Organic Acidemia.	Evaluate the Long Term Effectiveness & Safety of the Use of Carglumic Acid (Carbaglu®) in Patients W ...	Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA)	Drug: Carglumic Acid (Carbaglu®)	National Taiwan University Hospital	NULL	Enrolling by invitation	18 Years	N/A	All	5	N/A	Taiwan
3	NCT04176523 (ClinicalTrials.gov)	January 15, 2019	20/11/2019	Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods ...	Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods ...	Methylmalonic Acidemia;Propionic Acidemia	Drug: Carglumic Acid	Recordati Rare Diseases	NULL	Recruiting	6 Months	99 Years	All	75		France;Germany;Italy;Norway;Spain;Sweden;United Kingdom
4	NCT02426775 (ClinicalTrials.gov)	November 2015	22/4/2015	Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia	Randomized Multicentre Comparative Trial to Evaluate the Long Term Effectiveness of the Use of Carba ...	Propionic Acidemia;Methylmalonic Acidemia	Drug: Carglumic Acid	King Abdullah International Medical Research Center	NULL	Completed	N/A	15 Years	All	33	Phase 3	Saudi Arabia
5	NCT01599286 (ClinicalTrials.gov)	September 2012	11/5/2012	Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia	Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia	Propionic Acidemia, Type I and/or Type II;Methylmalonic Acidemia;Carbamoyl-Phosphate Synthase I Defi ...	Drug: Carbaglu;Drug: Placebo;Drug: Standard of Care Treatment	Mendel Tuchman	Children's National Research Institute;Boston Children's Hospital;University Hospitals Cleveland Med ...	Active, not recruiting	N/A	99 Years	All	114	Phase 2	United States

First Previous1Next Last

先頭へ

246. メチルマロン酸血症

臨床試験数 : 23 / 薬物数 : 31 - (DrugBank : 8) / 標的遺伝子数 : 17 - 標的パスウェイ数 : 23

diseases per page:

Showing 1 to 5 of 5 diseases

Filter by

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT05040178 (ClinicalTrials.gov)	June 30, 2022	16/6/2021	An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics	A Non-Interventional Post-Authorization Safety Study (PASS) of Carbaglu® for the Treatment of Hypera ...	Hyperammonemia;Methylmalonic Acidemia;Propionic Acidemia	Drug: Carglumic Acid	Recordati Rare Diseases	Target PharmaSolutions, Inc.	Recruiting	N/A	N/A	All	20		United States
2	NCT04284917 (ClinicalTrials.gov)	November 28, 2019	24/2/2020	Long-term Efficacy of Carglumic Acid in Organic Acidemia.	Evaluate the Long Term Effectiveness & Safety of the Use of Carglumic Acid (Carbaglu®) in Patients W ...	Propionic Acidemia (PA) , Methylmalonic Acidemia (MMA)	Drug: Carglumic Acid (Carbaglu®)	National Taiwan University Hospital	NULL	Enrolling by invitation	18 Years	N/A	All	5	N/A	Taiwan
3	NCT04176523 (ClinicalTrials.gov)	January 15, 2019	20/11/2019	Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods ...	Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods ...	Methylmalonic Acidemia;Propionic Acidemia	Drug: Carglumic Acid	Recordati Rare Diseases	NULL	Recruiting	6 Months	99 Years	All	75		France;Germany;Italy;Norway;Spain;Sweden;United Kingdom
4	NCT02426775 (ClinicalTrials.gov)	November 2015	22/4/2015	Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia	Randomized Multicentre Comparative Trial to Evaluate the Long Term Effectiveness of the Use of Carba ...	Propionic Acidemia;Methylmalonic Acidemia	Drug: Carglumic Acid	King Abdullah International Medical Research Center	NULL	Completed	N/A	15 Years	All	33	Phase 3	Saudi Arabia
5	NCT01599286 (ClinicalTrials.gov)	September 2012	11/5/2012	Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia	Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia	Propionic Acidemia, Type I and/or Type II;Methylmalonic Acidemia;Carbamoyl-Phosphate Synthase I Defi ...	Drug: Carbaglu;Drug: Placebo;Drug: Standard of Care Treatment	Mendel Tuchman	Children's National Research Institute;Boston Children's Hospital;University Hospitals Cleveland Med ...	Active, not recruiting	N/A	99 Years	All	114	Phase 2	United States

First Previous1Next Last

先頭へ