Modified mRNA encoding human methylmalonyl-coenzyme A mutase ( DrugBank: Coenzyme A, Methylmalonyl-coenzyme A )

1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
246	メチルマロン酸血症	1

246. メチルマロン酸血症

臨床試験数 : 23 / 薬物数 : 31 - (DrugBank : 8) / 標的遺伝子数 : 17 - 標的パスウェイ数 : 23

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2020-004980-24-NL (EUCTR)		28/07/2022	A clinical study to evaluate mRNA-3705 in Patients with MMA	A Global, Phase 1/2, Open-Label, Dose Optimization Study to Evaluate the Safety, Tolerability, Pharm ...	Isolated Methylmalonic Acidemia Due to Methylmalonyl-CoA Mutase Deficiency;Therapeutic area: Body pr ...	Product Name: mRNA-3705 INN or Proposed INN: NA Other descriptive name: Modified mRNA encoding human m ...	ModernaTX, Inc.	NULL	NA			Female: yes Male: yes	33	Phase 1;Phase 2	France;United States;Canada;Spain;Australia;Netherlands;United Kingdom;Switzerland

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