Enzyme Replacement Agent ( DrugBank: - )

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1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
256	筋型糖原病	1

256. 筋型糖原病

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臨床試験数 : 180 /  薬物数 : 133 - (DrugBank : 29) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 105

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03045042 (ClinicalTrials.gov)	April 2017	27/1/2017	Search for Serum/Plasma Biomarkers in Pompe's Disease	Search for Serum/Plasma Biomarkers in Pompe's Disease	Late Onset Pompe Disease;Pompe Disease	Drug: Enzyme Replacement Agent	Fundació Institut de Recerca de l'Hospital de la Santa Creu i Sant Pau	Genzyme, a Sanofi Company	Not yet recruiting	2 Years	N/A	All	35	N/A	Spain