Blinded CDCA 250 mg TID ( DrugBank: CDCA )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
263脳腱黄色腫症1

263. 脳腱黄色腫症


臨床試験数 : 6 薬物数 : 11 - (DrugBank : 2) / 標的遺伝子数 : 2 - 標的パスウェイ数 : 4
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04270682
(ClinicalTrials.gov)
January 31, 202012/2/2020Study to Evaluate Patients With Cerebrotendinous Xanthomatosis (RESTORE)A Phase 3 Study to Evaluate the Effects of Chenodeoxycholic Acid in Adult and Pediatric Patients With Cerebrotendinous XanthomatosisCTXDrug: Blinded CDCA 250 mg TID;Drug: Placebo;Drug: Open-Label CDCA 250 mg TID;Drug: Rescue Medication CDCA 250 mg TID;Drug: CDCA Weight-Based Dose TIDTravere Therapeutics, Inc.NULLRecruiting1 MonthN/AAll12Phase 3United States;Brazil