RAAV9-CB6-AspA ( DrugBank: - )

1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
307	カナバン病	1

307. カナバン病

臨床試験数 : 6 / 薬物数 : 11 - (DrugBank : 5) / 標的遺伝子数 : 2 - 標的パスウェイ数 : 2

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT05317780 (ClinicalTrials.gov)	February 10, 2020	24/3/2022	Canavan-Single Patient IND	Expanded Access Trial of Systemic Delivery of Aspartoacylase ASPA (rAAV9-CB6-AspA) Gene Vector in a ...	Canavan Disease	Drug: rAAV9-CB6-AspA	Barry J. Byrne	University of Miami;University of Massachusetts, Worcester	Available	18 Months	24 Months	Male			United States