PTR-01 ( DrugBank: - )

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1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
36	表皮水疱症	3

36. 表皮水疱症

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臨床試験数 : 163 /  薬物数 : 185 - (DrugBank : 46) / 標的遺伝子数 : 50 - 標的パスウェイ数 : 125

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT05143190 (ClinicalTrials.gov)	December 2, 2021	9/11/2021	Extension Study to PTR-01-002 (A Study in Recessive Dystrophic Epidermolysis Bullosa (RDEB) Patients Previously Treated With PTR-01)	A Phase 2b Open-Label Study of PTR-01 in Recessive Dystrophic Epidermolysis Bullosa (RDEB) Patients Previously Treated With PTR-01 in Study PTR-01-002	Recessive Dystrophic Epidermolysis Bullosa	Drug: PTR-01	Phoenix Tissue Repair, Inc.	Phoenix Tissue Repair, a BridgeBio company	Completed	12 Years	N/A	All	2	Phase 2	United States
2	NCT04599881 (ClinicalTrials.gov)	October 15, 2020	8/10/2020	A Study of PTR-01 in Recessive Dystrophic Epidermolysis Bullosa	A Phase 2 Open-Label Study of PTR-01 in Patients With Recessive Dystrophic Epidermolysis Bullosa (RDEB)	Recessive Dystrophic Epidermolysis Bullosa	Drug: PTR-01	Phoenix Tissue Repair, Inc.	NULL	Completed	12 Years	N/A	All	6	Phase 2	United States
3	NCT03752905 (ClinicalTrials.gov)	January 9, 2019	19/11/2018	A Phase 1/2 Trial of PTR-01 in Adult Patients With Recessive Dystrophic Epidermolysis Bullosa (RDEB)	A Phase 1/2 Randomized, Saline-Controlled, Single-Blind, Multiple Ascending Dose, Dose-Escalation, Multi-Center Trial of PTR-01 in Adult Patients With Recessive Dystrophic Epidermolysis Bullosa (RDEB)	Recessive Dystrophic Epidermolysis Bullosa	Drug: PTR-01;Drug: Normal saline	Phoenix Tissue Repair, Inc.	NULL	Completed	16 Years	N/A	All	12	Phase 1/Phase 2	United States