Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
65原発性免疫不全症候群2

65. 原発性免疫不全症候群


臨床試験数 : 500 薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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Inclusion_
agemin
Inclusion_
agemax
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gender
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size
PhaseCountries
1NCT01347346
(ClinicalTrials.gov)
May 20113/5/2011Gene Therapy for WASPhase I/II Clinical Trial of Haematopoietic Stem Cell Gene Therapy for the Wiskott-Aldrich SyndromeWiskott-Aldrich SyndromeGenetic: Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS geneGenethonHôpital Necker-Enfants MaladesCompletedN/AN/AMale5Phase 1/Phase 2France
2NCT01347242
(ClinicalTrials.gov)
March 20113/5/2011Gene Therapy for Wiskott-Aldrich Syndrome (WAS)Phase I/II Clinical Trial of Haematopoietic Stem Cell Gene Therapy for the Wiskott-Aldrich SyndromeWiskott-Aldrich SyndromeGenetic: Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS geneGenethonGreat Ormond Street Hospital for Children NHS Foundation Trust;Institute of Child HealthCompletedN/AN/AMale6Phase 1/Phase 2United Kingdom