Lentiviral vector transduced CD34+ cells ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
65原発性免疫不全症候群2

65. 原発性免疫不全症候群


臨床試験数 : 500 薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT03601286
(ClinicalTrials.gov)
December 21, 201822/2/2018Lentiviral Gene Therapy for X-linked Severe Combined ImmunodeficiencyPhase I/II Study of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted BusulfanSevere Combined Immunodeficiency, X-LinkedDrug: Lentiviral vector transduced CD34+ cellsGreat Ormond Street Hospital for Children NHS Foundation TrustNULLRecruiting8 Weeks5 YearsMale5Phase 1United Kingdom
2NCT01381003
(ClinicalTrials.gov)
November 201123/6/2011Lentiviral Gene Therapy for X-Linked Chronic Granulomatous Disease (X-CGD)Phase I/II Gene Therapy Protocol for X-Linked Chronic Granulomatous DiseaseGranulomatous Disease, Chronic, X-linked, VariantGenetic: pCCLchimGp91s lentiviral vector transduced CD34+ cells infusionGreat Ormond Street Hospital for Children NHS Foundation TrustNULLWithdrawnN/A30 YearsMale0Phase 1/Phase 2United Kingdom