Retroviral SF71-gp91phox transduced CD34+ cells ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
65原発性免疫不全症候群2

65. 原発性免疫不全症候群


臨床試験数 : 500 薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT00927134
(ClinicalTrials.gov)
June 200422/6/2009Gene Therapy for X-linked Chronic Granulomatous Disease (CGD) in ChildrenPhase I/II Gene Therapy Study for X-linked Chronic Granulomatous Disease in ChildrenChronic Granulomatous DiseaseGenetic: retroviral SF71-gp91phox transduced CD34+ cellsUniversity of ZurichGoethe UniversityCompleted1 Year18 YearsMale2Phase 1/Phase 2Switzerland
2NCT00564759
(ClinicalTrials.gov)
January 200426/11/2007Gene Therapy for Chronic Granulomatous DiseasePhase I/II Gene Therapy Study for X-Linked Chronic Granulomatous DiseaseGranulomatous Disease, ChronicDrug: retroviral SF71-gp91phox transduced CD34+ cellsJohann Wolfgang Goethe University HospitalsGerman Federal Ministry of Education and ResearchActive, not recruiting18 YearsN/AMale2Phase 1/Phase 2Germany