Somatic gene-therapy by X-CGD ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
65原発性免疫不全症候群1

65. 原発性免疫不全症候群


臨床試験数 : 500 薬物数 : 614 - (DrugBank : 119) / 標的遺伝子数 : 92 - 標的パスウェイ数 : 217
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1EUCTR2012-001725-26-DE
(EUCTR)
12/03/201318/12/2012A Phase I/II Gene Therapy trial for X-CGD with a SIN gamma retroviral vectorA Phase I/II Gene Therapy trial for X-CGD with a SIN gamma retroviral vector - gene therapy for X-CGD Chronic granulomatous disease (CGD) is a congenital immunodeficiency, in which neutrophil granulocytes and monocytes are not capable of producing reactive oxygen species and therefore are unable to kill phagocytized bacteria or fungi.
MedDRA version: 14.1;Level: PT;Classification code 10008906;Term: Chronic granulomatous disease;System Organ Class: 10010331 - Congenital, familial and genetic disorders;Therapeutic area: Diseases [C] - Blood and lymphatic diseases [C15]
Product Name: genetically modified autologous blood stem cells
Product Code: somatic gene-therapy by X-CGD
INN or Proposed INN: G1XCG
Other descriptive name: Genetically modified autologous blood stem cells
Johann Wolfgang Goethe-UniversityNULLNot RecruitingFemale: yes
Male: yes
5Phase 1;Phase 2Germany