4D-125 IVT Injection ( DrugBank: - )


1 disease
告示番号疾患名(ページ内リンク)臨床試験数
90網膜色素変性症1

90. 網膜色素変性症


臨床試験数 : 147 薬物数 : 176 - (DrugBank : 43) / 標的遺伝子数 : 49 - 標的パスウェイ数 : 110
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04517149
(ClinicalTrials.gov)
June 9, 202014/8/20204D-125 in Patients With X-Linked Retinitis Pigmentosa (XLRP)An Open-label, Phase 1/2 Trial of Gene Therapy 4D-125 in Males With X-linked Retinitis Pigmentosa (XLRP) Caused by Mutations in the RPGR GeneX-Linked Retinitis PigmentosaBiological: 4D-125 IVT Injection;Other: Observational4D Molecular TherapeuticsNULLActive, not recruiting12 YearsN/AMale21Phase 1/Phase 2United States