DDrare: Database of Drug Development for Rare Diseases

333. ハッチンソン・ギルフォード症候群
［臨床試験数：7，薬物数：8（DrugBank：3），標的遺伝子数：4，標的パスウェイ数：6］

Searched query = "Hutchinson-Gilford syndrome", "Hutchinson-Gilford progeria syndrome", "HGPS"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

Drug = Lonafarnib; Lonafarnib, Zoledronic Acid, and Pravastatin; Pravastatin; Progerinin; Umbilical Cord Blood Unit; Zoledronic Acid; Zoledronic acid; Zoledronic acid, pravastatin

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03871972 (ClinicalTrials.gov)	March 5, 2019	7/3/2019	Umbilical Cord Blood Transfusion in Progeria Syndrome	Safety and Efficacy of Umbilical Cord Blood Transfusion in Patients With Hutchinson-Gilford Progeria Syndrome	Hutchinson-Gilford Progeria Syndrome	Drug: Umbilical Cord Blood Unit	Bundang CHA Hospital	NULL	Completed	N/A	N/A	All	2	Phase 1;Phase 2	Korea, Republic of

No.

TrialID

Date_
enrollment

Date_
registration

Public_title

Scientific_title

Condition

Intervention

Primary_
sponsor

Secondary_
sponsor

Recruitment_
Status

Inclusion_
agemin

Inclusion_
agemax

Inclusion_
gender

Target_
size

Phase

Countries

NCT03871972
(ClinicalTrials.gov)

March 5, 2019

7/3/2019

Umbilical Cord Blood Transfusion in Progeria Syndrome

Safety and Efficacy of Umbilical Cord Blood Transfusion in Patients With Hutchinson-Gilford Progeria Syndrome

Hutchinson-Gilford Progeria Syndrome

Drug: Umbilical Cord Blood Unit

Bundang CHA Hospital

NULL

Completed

N/A

All

Phase 1;Phase 2

Korea, Republic of