113. 筋ジストロフィー Muscular dystrophy Clinical trials / Disease details

臨床試験数 : 622 / 薬物数 : 485 - (DrugBank : 99) / 標的遺伝子数 : 59 - 標的パスウェイ数 : 168

33 trials found

diseases per page:

Showing 1 to 10 of 33 diseases

Filter by

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2018-001762-42-NO (EUCTR)	04/03/2022	02/12/2021	A research study to compare different doses of a new investigational medicinal product for treatment ...	A Randomized, Double-Blind, Dose Finding and Comparison Study of the Safety and Efficacy of a High D ...	Duchenne Muscular Dystrophy MedDRA version: 20.0;Level: PT;Classification code 10013801;Term: Duchen ...	Product Name: Eteplirsen Product Code: AVI-4658 INN or Proposed INN: ETEPLIRSEN	Sarepta Therapeutics, Inc.	NULL	Authorised-recruitment may be ongoing or finished			Female: no Male: yes	154	Phase 3	United States;Serbia;Taiwan;Greece;Spain;Ukraine;Ireland;Russian Federation;Colombia;Italy;Switzerla ...
2	EUCTR2018-001762-42-GR (EUCTR)	01/02/2022	01/12/2021	A research study to compare different doses of a new investigational medicinal product for treatment ...	A Randomized, Double-Blind, Dose Finding and Comparison Study of the Safety and Efficacy of a High D ...	Duchenne Muscular Dystrophy MedDRA version: 20.0;Level: PT;Classification code 10013801;Term: Duchen ...	Product Name: Eteplirsen Product Code: AVI-4658 INN or Proposed INN: ETEPLIRSEN	Sarepta Therapeutics, Inc.	NULL	Authorised-recruitment may be ongoing or finished			Female: no Male: yes	154	Phase 3	United States;Serbia;Taiwan;Greece;Spain;Ukraine;Ireland;Russian Federation;Colombia;Italy;Switzerla ...
3	EUCTR2018-001762-42-DE (EUCTR)	29/10/2020	01/10/2019	A research study to compare different doses of a new investigational medicinal product for treatment ...	A Randomized, Double-Blind, Dose Finding and Comparison Study of the Safety and Efficacy of a High D ...	Duchenne Muscular Dystrophy MedDRA version: 20.0;Level: PT;Classification code 10013801;Term: Duchen ...	Product Name: Eteplirsen Product Code: AVI-4658 INN or Proposed INN: ETEPLIRSEN	Sarepta Therapeutics, Inc.	NULL	Not Recruiting			Female: no Male: yes	154	Phase 3	United States;Serbia;Taiwan;Greece;Spain;Ukraine;Ireland;Russian Federation;Colombia;Switzerland;Fra ...
4	EUCTR2018-001762-42-NL (EUCTR)	20/07/2020	21/07/2020	A research study to compare different doses of a new investigational medicinal product for treatment ...	A Randomized, Double-Blind, Dose Finding and Comparison Study of the Safety and Efficacy of a High D ...	Duchenne Muscular Dystrophy MedDRA version: 20.0;Level: PT;Classification code 10013801;Term: Duchen ...	Product Name: Eteplirsen Product Code: AVI-4658 INN or Proposed INN: ETEPLIRSEN	Sarepta Therapeutics, Inc.	NULL	Authorised-recruitment may be ongoing or finished			Female: no Male: yes	152	Phase 3	Korea, Republic of;Sweden;New Zealand;Netherlands;Germany;Norway;Australia;Denmark;Belgium;Poland;Ca ...
5	NCT03992430 (ClinicalTrials.gov)	July 13, 2020	18/6/2019	A Study to Compare Safety and Efficacy of a High Dose of Eteplirsenin Duchenne Muscular Dystrophy (D ...	A Randomized, Double-Blind, Dose Finding and Comparison Study of the Safety and Efficacy of a High D ...	Muscular Dystrophy, Duchenne	Drug: Eteplirsen	Sarepta Therapeutics, Inc.	NULL	Active, not recruiting	7 Years	13 Years	Male	152	Phase 3	United States;Canada;Korea, Republic of;Taiwan
6	EUCTR2018-001762-42-SE (EUCTR)	27/04/2020	26/09/2019	A research study to compare different doses of a new investigational medicinal product for treatment ...	A Randomized, Double-Blind, Dose Finding and Comparison Study of the Safety and Efficacy of a High D ...	Duchenne Muscular Dystrophy MedDRA version: 20.0;Level: PT;Classification code 10013801;Term: Duchen ...	Product Name: Eteplirsen Product Code: AVI-4658 INN or Proposed INN: ETEPLIRSEN	Sarepta Therapeutics, Inc.	NULL	Not Recruiting			Female: no Male: yes	152	Phase 3	United States;Taiwan;Spain;Ireland;Turkey;Russian Federation;Chile;Colombia;United Kingdom;Italy;Fra ...
7	EUCTR2018-001762-42-IE (EUCTR)	03/04/2020	01/07/2019	A research study to compare different doses of a new investigational medicinal product for treatment ...	A Randomized, Double-Blind, Dose Finding and Comparison Study of the Safety and Efficacy of a High D ...	Duchenne Muscular Dystrophy MedDRA version: 20.0;Level: PT;Classification code 10013801;Term: Duchen ...	Product Name: Eteplirsen Product Code: AVI-4658 INN or Proposed INN: ETEPLIRSEN	Sarepta Therapeutics, Inc.	NULL	Authorised-recruitment may be ongoing or finished			Female: no Male: yes	154	Phase 3	United States;Serbia;Taiwan;Greece;Spain;Ukraine;Ireland;Russian Federation;Colombia;Italy;Switzerla ...
8	NCT04179409 (ClinicalTrials.gov)	February 18, 2020	12/8/2019	A 48-Week, Open Label, Study to Evaluate the Efficacy and Safety of Casimersen, Eteplirsenand Golodi ...	A 48-Week, Open Label, Study to Evaluate the Efficacy and Safety of Casimersen, Eteplirsenand Golodi ...	Duchenne Muscular Dystrophy	Drug: Casimersen;Drug: Eteplirsen;Drug: Golodirsen	Kevin Flanigan	Sarepta Therapeutics, Inc.	Active, not recruiting	6 Months	N/A	Male	3	Phase 2	United States
9	EUCTR2018-001762-42-DK (EUCTR)	18/12/2019	30/10/2019	A research study to compare different doses of a new investigational medicinal product for treatment ...	A Randomized, Double-Blind, Dose Finding and Comparison Study of the Safety and Efficacy of a High D ...	Duchenne Muscular Dystrophy MedDRA version: 20.0;Level: PT;Classification code 10013801;Term: Duchen ...	Trade Name: Exondys 51 Product Name: Eteplirsen Product Code: AVI-4658 INN or Proposed INN: ETEPLIRSEN	Sarepta Therapeutics, Inc.	NULL	Not Recruiting			Female: no Male: yes	154	Phase 3	United States;Serbia;Taiwan;Greece;Spain;Ukraine;Ireland;Russian Federation;Colombia;Italy;Switzerla ...
10	EUCTR2018-001762-42-ES (EUCTR)	29/10/2019	09/08/2019	A research study to compare different doses of a new investigational medicinal product for treatment ...	A Randomized, Double-Blind, Dose Finding and Comparison Study of the Safety and Efficacy of a High D ...	Duchenne Muscular Dystrophy MedDRA version: 20.1;Level: PT;Classification code 10052655;Term: Duchen ...	Trade Name: Exondys 51 Product Name: Eteplirsen Product Code: AVI-4658 INN or Proposed INN: ETEPLIRSEN	Sarepta Therapeutics, Inc.	NULL	Authorised-recruitment may be ongoing or finished			Female: no Male: yes	152	Human pharmacology (Phase 1): no Therapeutic exploratory (Phase 2): no Therapeutic confirmatory - (P ...	Taiwan;Hong Kong;Spain;Ireland;Turkey;Russian Federation;Chile;Colombia;Italy;United Kingdom;France; ...

First Previous1 2 3 4Next Last