120. 遺伝性ジストニア Hereditary dystonia Clinical trials / Disease details


臨床試験数 : 25 薬物数 : 21 - (DrugBank : 4) / 標的遺伝子数 : 2 - 標的パスウェイ数 : 2

  
1 trial found
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1NCT03726996
(ClinicalTrials.gov)
January 14, 201929/10/2018Desipramine in Infantile Neuroaxonal Dystrophy (INAD).Novel Off-label Use of Desipramine in Infantile Neuroaxonal Dystrophy: Targeting the Sphingolipid Metabolism Pathway to Reduce Accumulation of Ceramide.Infantile Neuroaxonal DystrophyDrug: DesipramineDuke UniversityNULLTerminated3 Years17 YearsAll4Phase 4United States