DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
164. 眼皮膚白皮症
Oculocutaneous albinism
Clinical trials
/
Disease details
臨床試験数
:
15
/
薬物数
:
57
- (
DrugBank
:
34
) /
標的遺伝子数
:
35
-
標的パスウェイ数
:
139
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No.
TrialID
Date_
enrollment
Date_
registration
Public_title
Scientific_title
Condition
Intervention
Primary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
Phase
Countries
1
NCT01838655
(
ClinicalTrials.gov
)
April 16, 2013
20/4/2013
Nitisinone
for Type 1B Oculocutaneous Albinism
A Pilot Study of
Nitisinone
in the Treatment of Oculocutaneous Albinism, Type 1B
Albinism;Vision Loss
Drug:
Nitisinone
National Eye Institute (NEI)
National Human Genome Research Institute (NHGRI)
Completed
18 Years
N/A
All
5
Phase 1/Phase 2
United States