170. オクシピタル・ホーン症候群 Occipital horn syndrome Clinical trials / Disease details


臨床試験数 : 2 薬物数 : 4 - (DrugBank : 3) / 標的遺伝子数 : 9 - 標的パスウェイ数 : 14

  
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PhaseCountries
1NCT04977388
(ClinicalTrials.gov)
July 12, 20219/7/2021NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Occipital Horn SyndromePhase I/II Study of NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Adults With Occipital Horn Syndrome: Double-blind Placebo-controlled Randomized Crossover Clinical TrialMenkes Disease;Occipital Horn SyndromeDrug: Droxidopa;Other: PlaceboStephen G. Kaler, MDNULLRecruiting18 Years50 YearsAll6Phase 1/Phase 2United States
2NCT00811785
(ClinicalTrials.gov)
February 27, 200918/12/2008Molecular Bases of Response to Copper Treatment in Menkes Disease, Related Phenotypes, and Unexplained Copper DeficiencyMolecular Bases of Response to Copper Treatment in Menkes Disease, Related Phenotypes, and Unexplained Copper DeficiencyMenkes Disease;Occipital Horn Syndrome;Unexplained Copper DeficiencyDrug: Copper HistidineCyprium Therapeutics, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD);National Center for Complementary and Integrative Health (NCCIH)CompletedN/A80 YearsAll93Phase 3United States