170. オクシピタル・ホーン症候群 Occipital horn syndrome Clinical trials / Disease details
臨床試験数 : 2 / 薬物数 : 4 - (DrugBank : 3) / 標的遺伝子数 : 9 - 標的パスウェイ数 : 14
No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
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1 | NCT04977388 (ClinicalTrials.gov) | July 12, 2021 | 9/7/2021 | NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Occipital Horn Syndrome | Phase I/II Study of NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Adults With Occipital Horn Syndrome: Double-blind Placebo-controlled Randomized Crossover Clinical Trial | Menkes Disease;Occipital Horn Syndrome | Drug: Droxidopa;Other: Placebo | Stephen G. Kaler, MD | NULL | Recruiting | 18 Years | 50 Years | All | 6 | Phase 1/Phase 2 | United States |
2 | NCT00811785 (ClinicalTrials.gov) | February 27, 2009 | 18/12/2008 | Molecular Bases of Response to Copper Treatment in Menkes Disease, Related Phenotypes, and Unexplained Copper Deficiency | Molecular Bases of Response to Copper Treatment in Menkes Disease, Related Phenotypes, and Unexplained Copper Deficiency | Menkes Disease;Occipital Horn Syndrome;Unexplained Copper Deficiency | Drug: Copper Histidine | Cyprium Therapeutics, Inc. | Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD);National Center for Complementary and Integrative Health (NCCIH) | Completed | N/A | 80 Years | All | 93 | Phase 3 | United States |