19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 854 / 薬物数 : 716 - (DrugBank : 105) / 標的遺伝子数 : 70 - 標的パスウェイ数 : 191

2 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03153319 (ClinicalTrials.gov)	June 5, 2017	11/5/2017	Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I and II	Phase 1/2 Study of the Effect of Adalimumabon Physical Function and Musculoskeletal Disease in Mucop ...	Mucopolysaccharidosis I;Mucopolysaccharidosis II	Drug: Adalimumab Injection [Humira];Drug: Saline Solution for Injection	Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center	NULL	Recruiting	5 Years	N/A	All	14	Phase 1/Phase 2	United States
2	NCT02437253 (ClinicalTrials.gov)	May 2015	5/5/2015	Effects of Adalimumab in Mucopolysaccharidosis Types I, II and VI	Pilot Study of the Effect of Adalimumabon Physical Function and Musculoskeletal Disease in Mucopolys ...	Mucopolysaccharidosis Type I;Mucopolysaccharidosis Type II;Mucopolysaccharidosis Type VI	Drug: Adalimumab;Other: Placebo	Los Angeles Biomedical Research Institute	NULL	Completed	5 Years	N/A	All	2	Phase 1/Phase 2	United States

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