19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details
臨床試験数 : 854 / 薬物数 : 716 - (DrugBank : 105) / 標的遺伝子数 : 70 - 標的パスウェイ数 : 191
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT04018755 (ClinicalTrials.gov) | February 23, 2019 | 1/7/2019 | Open-label Study of Anakinra in MPS III | Open-label Pilot Study of the Effects of Anakinra in Mucopolysaccharidosis (MPS) III | Mucopolysaccharidosis III | Biological: anakinra | Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center | Cure Sanfilippo Foundation;Swedish Orphan Biovitrum | Active, not recruiting | 4 Years | N/A | All | 20 | Phase 2/Phase 3 | United States |