19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 854 / 薬物数 : 716 - (DrugBank : 105) / 標的遺伝子数 : 70 - 標的パスウェイ数 : 191

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT04018755 (ClinicalTrials.gov)	February 23, 2019	1/7/2019	Open-label Study of Anakinra in MPS III	Open-label Pilot Study of the Effects of Anakinra in Mucopolysaccharidosis (MPS) III	Mucopolysaccharidosis III	Biological: anakinra	Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center	Cure Sanfilippo Foundation;Swedish Orphan Biovitrum	Active, not recruiting	4 Years	N/A	All	20	Phase 2/Phase 3	United States

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