19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 854 / 薬物数 : 716 - (DrugBank : 105) / 標的遺伝子数 : 70 - 標的パスウェイ数 : 191

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03639844 (ClinicalTrials.gov)	November 6, 2017	17/8/2018	BPX-501 T Cells Infused Post Stem Cell Transplant in Pediatrics With Non-Malignant Disorders Ineligi ...	Expanded Access Protocol for CaspaCIDe T Cells From An HLA-Partially Matched Related Donor After Neg ...	Hurler Syndrome;Inherited Metabolic Disorder;Lysosomal Storage Disorder;Metachromatic Leukodystrophy ...	Biological: rivogenlecleucel;Drug: rimiducid	Bellicum Pharmaceuticals	NULL	No longer available	3 Months	21 Years	All			United States

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