19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details


臨床試験数 : 854 薬物数 : 716 - (DrugBank : 105) / 標的遺伝子数 : 70 - 標的パスウェイ数 : 191

  
1 trial found
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agemin
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1NCT02124083
(ClinicalTrials.gov)
April 25, 201425/4/2014Phase 1/2 Study of Vorinostat Therapy in Niemann-Pick Disease, Type C1Phase 1/2 Study of Vorinostat Therapy in Niemann-Pick Disease, Type C1Neimann-Pick DiseaseDrug: VorinostatEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)Washington University School of Medicine;Weill Medical College of Cornell UniversityCompleted18 Years60 YearsAll12Phase 1/Phase 2United States