255. 複合カルボキシラーゼ欠損症 Multiple carboxylase deficiency Clinical trials / Disease details
臨床試験数 : 1 / 薬物数 : 1 - (DrugBank : 0) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| 1 | NCT03269045 (ClinicalTrials.gov) | August 31, 2013 | 28/8/2017 | Study of ORL-1B in Patients With Biotinidase Deficiency | An Open-label, Single-arm, Phase 2 Study of ORL-1B in Patients With Biotinidase Deficiency | Biotinidase Deficiency | Drug: ORL-1B | Orpha Labs | NULL | Completed | N/A | 18 Years | All | 20 | Phase 1/Phase 2 | NULL |